Bivalent binding and signaling characteristics of Leridistim, a novel chimeric dual agonist of interleukin-3 and granulocyte colony-stimulating factor receptors

Exp Hematol. 2001 Apr;29(4):416-24. doi: 10.1016/s0301-472x(01)00611-7.

Abstract

Leridistim is a member of a novel family of engineered chimeric cytokines, myelopoietins, that contain agonists of both interleukin-3 (IL-3) receptors (IL-3R) and granulocyte colony-stimulating factor (G-CSF) receptors (G-CSFR). To more clearly understand Leridistim's function at the molecular level, binding to both IL-3R and G-CSFR and subsequent signaling characteristics have been delineated. The affinity of Leridistim for the human G-CSFR was found to be comparable to that of native G-CSF (IC(50) = 0.96 nM and 1.0 nM, respectively). Both Leridistim and G-CSF induced receptor tyrosine phosphorylation to a similar maximal level. Compared with native recombinant human IL-3 (rhIL-3), Leridistim was found to possess higher affinity for the IL-3R alpha chain (IL-3Ralpha) (IC(50) = 85 nM and 162 nM, respectively). However, the increase in Leridistim binding affinity to the functional, high-affinity heterodimeric IL-3Ralphabeta(c) receptor is lower than that observed with rhIL-3 (85 nM and 14 nM vs 162 nM and 3.5 nM, respectively). Leridistim induced tyrosine phosphorylation of beta(c) to a level comparable to native IL-3, and the level of JAK2 tyrosine phosphorylation in cells expressing both IL-3R and G-CSFR was comparable to that observed with IL-3 or G-CSF alone. The ability of Leridistim to interact with IL-3R and G-CSFR simultaneously was demonstrated using surface plasmon resonance analysis. These studies were extended to demonstrate that Leridistim exhibited a higher affinity for the IL-3R on cells that express both the IL-3Ralphabeta(c) and the G-CSFR (IC(50) = 2 nM) compared with cells that contain the IL-3Ralphabeta(c) alone (IC(50) = 14 nM). Leridistim binds to both IL-3R and G-CSFR simultaneously and has been shown to activate both receptors. The bivalent avidity may explain the unique biologic effects and unexpected potency of Leridistim in hematopoietic cells compared with rhIL-3 or G-CSF alone or in combination.

Publication types

  • Comparative Study

MeSH terms

  • Animals
  • Antigens, CD34 / analysis
  • Bone Marrow Cells / immunology
  • Bone Marrow Cells / metabolism
  • Cell Line
  • Cricetinae
  • DNA / metabolism
  • DNA-Binding Proteins / metabolism
  • Dimerization
  • Electrophoresis
  • Granulocyte Colony-Stimulating Factor / metabolism
  • Granulocyte Colony-Stimulating Factor / pharmacology
  • Humans
  • Interleukin-3 / genetics
  • Interleukin-3 / metabolism*
  • Janus Kinase 2
  • Leukemia, Myeloid, Acute
  • Mice
  • Milk Proteins*
  • Phosphorylation
  • Phosphotyrosine / metabolism
  • Protein-Tyrosine Kinases / metabolism
  • Proto-Oncogene Proteins*
  • Receptors, Granulocyte Colony-Stimulating Factor / agonists*
  • Receptors, Granulocyte Colony-Stimulating Factor / genetics
  • Receptors, Granulocyte Colony-Stimulating Factor / metabolism
  • Receptors, Interleukin-3 / agonists*
  • Receptors, Interleukin-3 / genetics
  • Receptors, Interleukin-3 / metabolism
  • Recombinant Fusion Proteins / metabolism
  • Recombinant Proteins / metabolism
  • STAT5 Transcription Factor
  • Signal Transduction*
  • Surface Plasmon Resonance
  • Trans-Activators / metabolism
  • Transfection
  • Tumor Cells, Cultured

Substances

  • Antigens, CD34
  • DNA-Binding Proteins
  • Interleukin-3
  • Milk Proteins
  • Proto-Oncogene Proteins
  • Receptors, Granulocyte Colony-Stimulating Factor
  • Receptors, Interleukin-3
  • Recombinant Fusion Proteins
  • Recombinant Proteins
  • STAT5 Transcription Factor
  • Trans-Activators
  • Granulocyte Colony-Stimulating Factor
  • leridistim
  • Phosphotyrosine
  • DNA
  • Protein-Tyrosine Kinases
  • JAK2 protein, human
  • Jak2 protein, mouse
  • Janus Kinase 2