The use of steroid-sparing agents in steroid-sensitive nephrotic syndrome

Pediatr Nephrol. 2003 Sep;18(9):919-24. doi: 10.1007/s00467-003-1216-z. Epub 2003 Jul 23.

Abstract

Childhood nephrotic syndrome (NS) is frequently characterized by a relapsing course. There is no uniform agreement about the precise stage at which a steroid-sparing agent should be introduced to control the disease. In order to evaluate the treatment strategies and outcome of steroid-sensitive NS over the last 2 decades, a retrospective notes review was undertaken in a cohort of children treated at Great Ormond Street Children's Hospital between 1980 and 2000. From a population of 863 children with NS referred, 509 had frequently relapsing or steroid-dependent disease and 261 children received at least one steroid-sparing agent. Cyclophosphamide was the first choice in 178 patients and in 114 no further steroid-sparing agent was needed. Levamisole was prescribed as the first steroid-sparing agent for 65 children and disease control was achieved in 30%. Cyclosporin A was prescribed in 61 children and sustained remission was induced in 69%. It is concluded that cyclophosphamide is a potent agent in inducing sustained remission in steroid-sensitive NS. Levamisole and cyclosporin A have emerged as attractive steroid-sparing agents. Complications and major side effects of treatment are infrequent but occasionally fatal.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adolescent
  • Child
  • Child, Preschool
  • Glucocorticoids / administration & dosage*
  • Glucocorticoids / adverse effects*
  • Humans
  • Immunosuppressive Agents / therapeutic use
  • Infant
  • Nephrotic Syndrome / drug therapy*
  • Nephrotic Syndrome / pathology
  • Prednisolone / administration & dosage*
  • Prednisolone / adverse effects*
  • Recurrence
  • Remission Induction
  • Retrospective Studies
  • Treatment Outcome

Substances

  • Glucocorticoids
  • Immunosuppressive Agents
  • Prednisolone