Targeting BCL-2-related proteins in cancer therapy

Cancer Biol Ther. 2003 Jul-Aug;2(4 Suppl 1):S105-14.

Abstract

The BCL-2 family proteins are attractive targets for drug design. As pivotal regulators of apoptotic cell death, the logic of manipulating BCL-2 functions for anti-tumor effects is perhaps the strongest for any of the molecular targets proposed for cancer therapeutics. Moreover, elevated levels of anti-apoptotic proteins have been demonstrated in virtually every type of human cancer. BCL2-specific antisense oligonucleotides have shown broad anti-cancer activities in pre-clinical models and are currently in several phase III trials. Rational drug design to manipulate the functions of these proteins has been hampered by the lack of a clear understanding of biochemical or molecular functions. Initial efforts have been centered on disrupting protein-protein interactions within the BCL-2 homology (BH) family. Substantial progress in this task has been made using molecular modeling and drug leads.

Publication types

  • Review

MeSH terms

  • Apoptosis
  • Cell Line, Tumor
  • Clinical Trials as Topic
  • Cytochromes c / metabolism
  • Humans
  • Mitochondria / metabolism
  • Models, Biological
  • Models, Chemical
  • Neoplasms / drug therapy*
  • Neoplasms / pathology
  • Oligonucleotides, Antisense / pharmacology
  • Peptides / chemistry
  • Protein Structure, Tertiary
  • Proto-Oncogene Proteins c-bcl-2 / metabolism*
  • bcl-X Protein

Substances

  • BCL2L1 protein, human
  • Oligonucleotides, Antisense
  • Peptides
  • Proto-Oncogene Proteins c-bcl-2
  • bcl-X Protein
  • Cytochromes c