Simplified generation of high-titer retrovirus producer cells for clinically relevant retroviral vectors by reversible inclusion of a lox-P-flanked marker gene

Mol Ther. 2004 May;9(5):738-46. doi: 10.1016/j.ymthe.2004.02.010.

Abstract

Retroviral producer cells are generated by the introduction of a viral genome into "helper" cell lines containing all the necessary components for viral packaging and the release of infectious particles. The selection of high-titer vector producer cells is most efficient if the vector genome encodes a selectable marker, while it is extremely tedious to select high-titer producer clones if the transgene cannot be detected and selected directly. Here we describe the development of a screening system that uses reversible integration of lox-P-flanked eGFP as a qualitative and quantitative marker gene in two different vector systems, greatly facilitating the selection of viral producer cells. After selection and titration of high-titer viral producer cells based on eGFP expression, the eGFP gene could be removed from the provirus by transient introduction of Cre-recombinase into the producer cells, thus allowing the production of therapeutic relevant vectors expressing solely the gene of interest. However, after removal of the marker gene a slight but consistent increase in viral titers compared to the respective control vectors was found, independent of the transgene or backbone used. The single lox-P site retained in the vector backbone does not affect gene expression level or fidelity of RNA processing.

MeSH terms

  • Animals
  • Antigens, CD / genetics
  • Antigens, CD34 / genetics
  • Cell Culture Techniques
  • Gene Expression
  • Gene Rearrangement / genetics
  • Genetic Markers
  • Genetic Vectors / genetics*
  • Genetic Vectors / therapeutic use
  • Humans
  • Integrases / genetics
  • Integrases / metabolism*
  • Membrane Cofactor Protein
  • Membrane Glycoproteins / genetics
  • Mice
  • Proviruses / genetics
  • Proviruses / growth & development
  • Recombination, Genetic / genetics
  • Retroviridae / genetics*
  • Retroviridae / growth & development
  • Terminal Repeat Sequences / genetics
  • Viral Proteins / genetics
  • Viral Proteins / metabolism*

Substances

  • Antigens, CD
  • Antigens, CD34
  • CD46 protein, human
  • Genetic Markers
  • Mcp protein, mouse
  • Membrane Cofactor Protein
  • Membrane Glycoproteins
  • Viral Proteins
  • Cre recombinase
  • Integrases