Poly-beta amino ester-containing microparticles enhance the activity of nonviral genetic vaccines

Proc Natl Acad Sci U S A. 2004 Jun 29;101(26):9534-9. doi: 10.1073/pnas.0403549101. Epub 2004 Jun 21.

Abstract

Current nonviral genetic vaccine systems are less effective than viral vaccines, particularly in cancer systems where epitopes can be weakly immunogenic and antigen-presenting cell processing and presentation to T cells is down-regulated. A promising nonviral delivery method for genetic vaccines involves microencapsulation of antigen-encoding DNA, because such particles protect plasmid payloads and target them to phagocytic antigen-presenting cells. However, conventional microparticle formulations composed of poly lactic-co-glycolic acid take too long to release encapsulated payload and fail to induce high levels of target gene expression. Here, we describe a microparticle-based DNA delivery system composed of a degradable, pH-sensitive poly-beta amino ester and poly lactic-co-glycolic acid. These formulations generate an increase of 3-5 orders of magnitude in transfection efficiency and are potent activators of dendritic cells in vitro. When used as vaccines in vivo, these microparticle formulations, unlike conventional formulations, induce antigen-specific rejection of transplanted syngenic tumor cells.

Publication types

  • Research Support, Non-U.S. Gov't
  • Research Support, U.S. Gov't, Non-P.H.S.
  • Research Support, U.S. Gov't, P.H.S.

MeSH terms

  • Animals
  • Cancer Vaccines / administration & dosage
  • Cancer Vaccines / genetics
  • Cancer Vaccines / immunology
  • Cell Line, Tumor
  • Cells, Cultured
  • Dendritic Cells / immunology
  • Drug Delivery Systems / methods*
  • Esters / chemistry*
  • Gene Expression
  • Genes, Reporter / genetics
  • Glycolates / chemistry
  • Hydrogen-Ion Concentration
  • Lactic Acid
  • Mice
  • Mice, Inbred C57BL
  • Microspheres
  • Neoplasm Transplantation
  • Neoplasms / immunology
  • Piperazines / chemistry*
  • Polyesters / chemistry*
  • Polyglycolic Acid
  • Polylactic Acid-Polyglycolic Acid Copolymer
  • Polymers / chemistry*
  • Transfection / methods*
  • Vaccines, DNA / administration & dosage*
  • Vaccines, DNA / genetics*
  • Vaccines, DNA / immunology

Substances

  • Cancer Vaccines
  • Esters
  • Glycolates
  • Piperazines
  • Polyesters
  • Polymers
  • Vaccines, DNA
  • Polylactic Acid-Polyglycolic Acid Copolymer
  • Polyglycolic Acid
  • Lactic Acid