Successful adoptive transfer and in vivo expansion of human haploidentical NK cells in patients with cancer

Blood. 2005 Apr 15;105(8):3051-7. doi: 10.1182/blood-2004-07-2974. Epub 2005 Jan 4.

Abstract

We previously demonstrated that autologous natural killer (NK)-cell therapy after hematopoietic cell transplantation (HCT) is safe but does not provide an antitumor effect. We hypothesize that this is due to a lack of NK-cell inhibitory receptor mismatching with autologous tumor cells, which may be overcome by allogeneic NK-cell infusions. Here, we test haploidentical, related-donor NK-cell infusions in a nontransplantation setting to determine safety and in vivo NK-cell expansion. Two lower intensity outpatient immune suppressive regimens were tested: (1) low-dose cyclophosphamide and methylprednisolone and (2) fludarabine. A higher intensity inpatient regimen of high-dose cyclophosphamide and fludarabine (Hi-Cy/Flu) was tested in patients with poor-prognosis acute myeloid leukemia (AML). All patients received subcutaneous interleukin 2 (IL-2) after infusions. Patients who received lower intensity regimens showed transient persistence but no in vivo expansion of donor cells. In contrast, infusions after the more intense Hi-Cy/Flu resulted in a marked rise in endogenous IL-15, expansion of donor NK cells, and induction of complete hematologic remission in 5 of 19 poor-prognosis patients with AML. These findings suggest that haploidentical NK cells can persist and expand in vivo and may have a role in the treatment of selected malignancies used alone or as an adjunct to HCT.

Publication types

  • Clinical Trial
  • Research Support, U.S. Gov't, P.H.S.

MeSH terms

  • Acute Disease
  • Adoptive Transfer*
  • Carcinoma, Renal Cell / immunology
  • Carcinoma, Renal Cell / therapy
  • Cell Division / immunology
  • Haploidy
  • Hodgkin Disease / immunology
  • Hodgkin Disease / therapy
  • Humans
  • Immunotherapy / methods*
  • Kidney Neoplasms / immunology
  • Kidney Neoplasms / therapy
  • Killer Cells, Natural / cytology
  • Killer Cells, Natural / transplantation*
  • Leukemia, Myeloid / immunology
  • Leukemia, Myeloid / therapy*
  • Melanoma / immunology
  • Melanoma / therapy
  • Skin Neoplasms / immunology
  • Skin Neoplasms / therapy
  • Treatment Outcome