Increased hepatic transduction with reduced systemic dissemination and proinflammatory cytokines following hydrodynamic injection of helper-dependent adenoviral vectors

Mol Ther. 2005 Jul;12(1):99-106. doi: 10.1016/j.ymthe.2005.03.001.

Abstract

Hydrodynamic injection of helper-dependent adenoviral vectors (HDAd) in mice results in increased hepatic transduction, reduced splenic and pulmonary transduction, and reduced levels of the proinflammatory cytokines IL-6 and IL-12 compared to conventional injection. These results indicate that hepatic transduction by HDAd, at least alone, does not necessarily provoke a severe innate inflammatory response. Instead, they suggest that systemic vector dissemination may play a major role in the severity of the innate inflammatory response. These results further suggest that the safety and efficacy of HDAd-mediated, liver-directed gene therapy may be improved if the vector could be preferentially, if not exclusively, targeted to liver.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't
  • Research Support, U.S. Gov't, P.H.S.

MeSH terms

  • Adenoviridae*
  • Animals
  • Cytokines / metabolism*
  • Factor IX / genetics
  • Factor IX / metabolism
  • Genetic Vectors*
  • Humans
  • Kupffer Cells / metabolism
  • Liver / metabolism*
  • Lung / metabolism
  • Mice
  • Spleen / metabolism
  • Time Factors
  • Transduction, Genetic*
  • Transgenes

Substances

  • Cytokines
  • Factor IX