Efficient delivery of small interfering RNA to bone-metastatic tumors by using atelocollagen in vivo

Proc Natl Acad Sci U S A. 2005 Aug 23;102(34):12177-82. doi: 10.1073/pnas.0501753102. Epub 2005 Aug 9.

Abstract

Silencing of gene expression by small interfering RNAs (siRNAs) is rapidly becoming a powerful tool for genetic analysis and represents a potential strategy for therapeutic product development. However, there are no reports of systemic delivery for siRNAs toward treatment of bone-metastatic cancer. Accordingly, we report here that i.v. injection of GL3 luciferase siRNA complexed with atelocollagen showed effective reduction of luciferase expression from bone-metastatic prostate tumor cells developed in mouse thorax, jaws, and/or legs. We also show that the siRNA/atelocollagen complex can be efficiently delivered to tumors 24 h after injection and can exist intact at least for 3 days. Furthermore, atelocollagen-mediated systemic administration of siRNAs such as enhancer of zeste homolog 2 and phosphoinositide 3'-hydroxykinase p110-alpha-subunit, which were selected as candidate targets for inhibition of bone metastasis, resulted in an efficient inhibition of metastatic tumor growth in bone tissues. In addition, upregulation of serum IL-12 and IFN-alpha levels was not associated with the in vivo administration of the siRNA/atelocollagen complex. Thus, for treatment of bone metastasis of prostate cancer, an atelocollagen-mediated systemic delivery method could be a reliable and safe approach to the achievement of maximal function of siRNA.

Publication types

  • Comparative Study
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Animals
  • Bone Neoplasms / secondary*
  • Bone Neoplasms / therapy*
  • Cell Line, Tumor
  • Collagen / administration & dosage*
  • DNA-Binding Proteins / genetics
  • Drug Carriers / therapeutic use
  • Enhancer of Zeste Homolog 2 Protein
  • Gene Expression Regulation, Neoplastic / genetics*
  • Genetic Therapy / methods*
  • Humans
  • Luciferases / metabolism
  • Male
  • Mice
  • Phosphatidylinositol 3-Kinases / genetics
  • Polycomb Repressive Complex 2
  • Prostatic Neoplasms / pathology*
  • RNA, Small Interfering / administration & dosage
  • RNA, Small Interfering / genetics
  • RNA, Small Interfering / therapeutic use*
  • Reverse Transcriptase Polymerase Chain Reaction
  • Transcription Factors / genetics

Substances

  • DNA-Binding Proteins
  • Drug Carriers
  • RNA, Small Interfering
  • Transcription Factors
  • atelocollagen
  • Collagen
  • Luciferases
  • EZH2 protein, human
  • Enhancer of Zeste Homolog 2 Protein
  • Polycomb Repressive Complex 2
  • Phosphatidylinositol 3-Kinases