Crooked tail (Cd) model of human folate-responsive neural tube defects is mutated in Wnt coreceptor lipoprotein receptor-related protein 6

Proc Natl Acad Sci U S A. 2005 Sep 6;102(36):12843-8. doi: 10.1073/pnas.0501963102. Epub 2005 Aug 26.

Abstract

A cranial neural tube defect in Crooked tail (Cd) mice is prevented with prenatal dietary folic acid Cd positional cloning reveals a missense mutation of a highly conserved amino acid in the low density lipoprotein receptor-related protein 6 (Lrp6), a coreceptor required for Wnt canonical signaling. Molecular modeling predicts that Lrp6(Cd) alters a hinge region of the second YWTD beta-propeller domain. Mutant LRP6 binds to Wnt and Dickkopf1 (Dkk1) but not Mesd1, and Dkk1 cannot antagonize Wnt in Cd/Cd cells, resulting in hyperactivity. NIH 3T3 cells transfected with a mutant Lrp6 plasmid resist Dkk1 antagonism much like Cd/+ cells, confirming the significance of the mutation. The Lrp6 mutation in Cd mice provides evidence for a functional connection between Wnt signaling and folate rescue of neural tube defects.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, U.S. Gov't, P.H.S.

MeSH terms

  • Amino Acid Sequence
  • Animals
  • Embryo, Mammalian / embryology
  • Embryo, Mammalian / metabolism
  • Folic Acid / pharmacology*
  • Gene Expression Regulation, Developmental
  • Humans
  • Intercellular Signaling Peptides and Proteins / metabolism*
  • Low Density Lipoprotein Receptor-Related Protein-6
  • Mice
  • Mice, Inbred DBA
  • Models, Animal
  • Models, Molecular
  • Molecular Sequence Data
  • Mutation / genetics
  • Neural Tube Defects / metabolism*
  • Protein Structure, Tertiary
  • Proteins / genetics
  • Proteins / metabolism
  • Receptors, LDL / chemistry
  • Receptors, LDL / genetics*
  • Receptors, LDL / metabolism*
  • Sequence Alignment
  • Tail / embryology*
  • Tail / growth & development
  • Tail / metabolism*
  • Wnt Proteins

Substances

  • DKK1 protein, human
  • Dkk1 protein, mouse
  • Intercellular Signaling Peptides and Proteins
  • LRP6 protein, human
  • Low Density Lipoprotein Receptor-Related Protein-6
  • Lrp6 protein, mouse
  • Proteins
  • Receptors, LDL
  • Wnt Proteins
  • Folic Acid