Human alpha2-globin nonsense-mediated mRNA decay induced by a novel alpha-thalassaemia frameshift mutation at codon 22

Br J Haematol. 2006 Apr;133(1):98-102. doi: 10.1111/j.1365-2141.2006.05971.x.

Abstract

We describe a novel alpha-thalassaemia determinant in a 3-year-old girl presenting a mild microcytic and hypochromic anaemia, and normal haemoglobin A2 level. Molecular studies revealed heterozygosity for a novel microdeletion (-C) at codon 22 of the alpha2-globin gene. As the frameshift mutation generates a premature translation termination codon at position 48/49, we investigated the effect of the nonsense codon on the alpha2-globin gene expression. Although it does not affect RNA splicing, the premature nonsense codon induces accelerated mRNA degradation. To our knowledge, this is the first time the nonsense-mediated mRNA decay has been reported to occur in human alpha-globin mRNA.

Publication types

  • Case Reports
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Codon, Nonsense*
  • Female
  • Frameshift Mutation*
  • Gene Expression
  • Genetic Vectors / pharmacology
  • Genotype
  • Globins / genetics*
  • HeLa Cells
  • Humans
  • RNA Stability*
  • RNA, Messenger / genetics*
  • Reverse Transcriptase Polymerase Chain Reaction
  • Transfection
  • alpha-Thalassemia / blood
  • alpha-Thalassemia / genetics*

Substances

  • Codon, Nonsense
  • RNA, Messenger
  • Globins