High molecular response rate of polycythemia vera patients treated with pegylated interferon alpha-2a

Blood. 2006 Sep 15;108(6):2037-40. doi: 10.1182/blood-2006-03-009860. Epub 2006 May 18.

Abstract

V617F JAK2 mutation is a reliable molecular marker of polycythemia vera (PV), potentially useful to monitor the effect of treatments in this disease. In a phase 2 study of pegylated (peg) IFN-alpha-2a in PV, we performed prospective sequential quantitative evaluation of the percentage of mutated JAK2 allele (%V617F) by real-time polymerase chain reaction (PCR). The %V617F decreased in 24 (89%) of 27 treated patients, from a mean of 49% to a mean of 27% (mean decrease of 44%; P < .001), and no evidence for a plateau was observed. In one patient, mutant JAK2 was no longer detectable after 12 months. In 3 patients homozygous for the mutation, reappearance of 50% of wild-type allele was observed during treatment. The results seem to confirm the hypothesis that IFN-alpha preferentially targets the malignant clone in PV and show that %V617F assessment using a quantitative method may provide the first tool to monitor minimal residual disease in PV. This trial was registered at www.clinicaltrials.gov as #NCT00241241.

Publication types

  • Clinical Trial, Phase II
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adult
  • Aged
  • Female
  • Genetic Markers
  • Humans
  • Interferon alpha-2
  • Interferon-alpha / therapeutic use*
  • Janus Kinase 2
  • Male
  • Middle Aged
  • Point Mutation
  • Polycythemia Vera / drug therapy*
  • Polycythemia Vera / genetics*
  • Polyethylene Glycols / therapeutic use*
  • Protein-Tyrosine Kinases / genetics*
  • Proto-Oncogene Proteins / genetics*
  • Recombinant Proteins
  • Time Factors

Substances

  • Genetic Markers
  • Interferon alpha-2
  • Interferon-alpha
  • Proto-Oncogene Proteins
  • Recombinant Proteins
  • Polyethylene Glycols
  • Protein-Tyrosine Kinases
  • JAK2 protein, human
  • Janus Kinase 2
  • peginterferon alfa-2a

Associated data

  • ClinicalTrials.gov/NCT00241241