Novel oligodeoxynucleotide agonists of TLR9 containing N3-Me-dC or N1-Me-dG modifications

Nucleic Acids Res. 2006 Jun 23;34(11):3231-8. doi: 10.1093/nar/gkl430. Print 2006.

Abstract

Synthetic oligodeoxynucleotides containing unmethylated CpG motifs activate Toll-Like Receptor 9 (TLR9). Our previous studies have shown the role of hydrogen-bond donor and acceptor groups of cytosine and guanine in the CpG motif and identified synthetic immunostimulatory motifs. In the present study to elucidate the significance of N3-position of cytosine and N1-position of guanine in the CpG motif, we substituted C or G of a CpG dinucleotide with N3-Me-cytosine or N1-Me-guanine, respectively, in immunomodulatory oligodeoxynucleotides (IMOs). IMOs containing N-Me-cytosine or N-Me-guanine in C- or G-position, respectively, of the CpG dinucleotide showed activation of HEK293 cells expressing TLR9, but not TLR3, 7 or 8. IMOs containing N-Me-cytosine or N-Me-guanine modification showed activity in mouse spleen cell cultures, in vivo in mice, and in human cell cultures. In addition, IMOs containing N-Me-substitutions reversed antigen-induced Th2 immune responses towards a Th1-type in OVA-sensitized mouse spleen cell cultures. These studies suggest that TLR9 tolerates a methyl group at N1-position of G and a methyl group at N3-position of C may interfere with TLR9 activation to some extent. These are the first studies elucidating the role of N3-position of cytosine and N1-position of guanine in a CpG motif for TLR9 activation and immune stimulation.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adjuvants, Immunologic / chemical synthesis
  • Adjuvants, Immunologic / chemistry*
  • Adjuvants, Immunologic / pharmacology*
  • Animals
  • B-Lymphocytes / drug effects
  • B-Lymphocytes / immunology
  • Cell Line
  • Cells, Cultured
  • CpG Islands
  • Cytokines / biosynthesis
  • Deoxycytosine Nucleotides / chemistry
  • Deoxyguanine Nucleotides / chemistry
  • Female
  • Humans
  • Lymphocyte Activation
  • Mice
  • Mice, Inbred BALB C
  • Mice, Inbred C57BL
  • Oligodeoxyribonucleotides / chemical synthesis
  • Oligodeoxyribonucleotides / chemistry*
  • Oligodeoxyribonucleotides / pharmacology*
  • Spleen / cytology
  • Spleen / immunology
  • Splenomegaly / chemically induced
  • Th1 Cells / immunology
  • Toll-Like Receptor 9 / agonists*

Substances

  • Adjuvants, Immunologic
  • Cytokines
  • Deoxycytosine Nucleotides
  • Deoxyguanine Nucleotides
  • Oligodeoxyribonucleotides
  • Tlr9 protein, mouse
  • Toll-Like Receptor 9