In vitro resistance to the human immunodeficiency virus type 1 maturation inhibitor PA-457 (Bevirimat)

J Virol. 2006 Nov;80(22):10957-71. doi: 10.1128/JVI.01369-06. Epub 2006 Sep 6.

Abstract

3-O-(3',3'-dimethylsuccinyl)betulinic acid (PA-457 or bevirimat) potently inhibits human immunodeficiency virus type 1 (HIV-1) maturation by blocking a late step in the Gag processing pathway, specifically the cleavage of SP1 from the C terminus of capsid (CA). To gain insights into the mechanism(s) by which HIV-1 could evolve resistance to PA-457 and to evaluate the likelihood of such resistance arising in PA-457-treated patients, we sought to identify and characterize a broad spectrum of HIV-1 variants capable of conferring resistance to this compound. Numerous independent rounds of selection repeatedly identified six single-amino-acid substitutions that independently confer PA-457 resistance: three at or near the C terminus of CA (CA-H226Y, -L231F, and -L231M) and three at the first and third residues of SP1 (SP1-A1V, -A3T, and -A3V). We determined that mutations CA-H226Y, CA-L231F, CA-L231M, and SP1-A1V do not impose a significant replication defect on HIV-1 in culture. In contrast, mutations SP1-A3V and -A3T severely impaired virus replication and inhibited virion core condensation. The replication defect imposed by SP1-A3V was reversed by a second-site compensatory mutation in CA (CA-G225S). Intriguingly, high concentrations of PA-457 enhanced the maturation of SP1 residue 3 mutants. The different phenotypes associated with mutations that confer PA-457 resistance suggest the existence of multiple mechanisms by which HIV-1 can evolve resistance to this maturation inhibitor. These findings have implications for the ongoing development of PA-457 to treat HIV-1 infection in vivo.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, N.I.H., Intramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Amino Acid Substitution / genetics
  • Anti-HIV Agents / pharmacology*
  • Capsid Proteins / genetics
  • DNA Mutational Analysis
  • Drug Resistance, Viral / genetics*
  • HIV-1 / drug effects*
  • HIV-1 / genetics
  • HIV-1 / ultrastructure
  • Humans
  • Jurkat Cells
  • Microscopy, Electron, Transmission
  • Mutation, Missense
  • Succinates / pharmacology*
  • Suppression, Genetic
  • Triterpenes / pharmacology*
  • Viral Proteins / analysis
  • Viral Proteins / isolation & purification
  • Virion / ultrastructure
  • Virus Assembly / drug effects
  • Virus Replication / drug effects

Substances

  • Anti-HIV Agents
  • Capsid Proteins
  • Succinates
  • Triterpenes
  • Viral Proteins
  • bevirimat