Xanthurenic aciduria due to a mutation in KYNU encoding kynureninase

J Inherit Metab Dis. 2007 Apr;30(2):248-55. doi: 10.1007/s10545-007-0396-2. Epub 2007 Mar 1.

Abstract

Massive urinary excretion of xanthurenic acid, 3-hydroxykynurenine and kynurenine, known as xanthurenic aciduria or hydroxykynureninuria, in a young Somali boy suggested kynureninase deficiency. Mutation analysis of KYNU encoding kynureninase of the index case revealed homozygosity for a c.593 A > G substitution leading to a threonine-to-alanine (T198A) shift. A younger brother was found to have a similar excretion pattern and the same genotype. At present, neither of the two boys has symptoms of niacin deficiency. This is the first report linking xanthurenic aciduria to a mutation in the gene encoding kynureninase.

Publication types

  • Case Reports

MeSH terms

  • Adenine
  • Alanine
  • Amino Acid Metabolism, Inborn Errors / genetics*
  • Amino Acid Substitution
  • Child
  • DNA Mutational Analysis
  • Genotype
  • Guanine
  • Homozygote
  • Humans
  • Hydrolases / deficiency
  • Hydrolases / genetics*
  • Male
  • Mutation*
  • Pedigree
  • Threonine
  • Xanthurenates / urine*

Substances

  • Xanthurenates
  • Threonine
  • xanthurenic acid
  • Guanine
  • Hydrolases
  • kynureninase
  • Adenine
  • Alanine