Mutations in ZDHHC9, which encodes a palmitoyltransferase of NRAS and HRAS, cause X-linked mental retardation associated with a Marfanoid habitus

Am J Hum Genet. 2007 May;80(5):982-7. doi: 10.1086/513609. Epub 2007 Mar 20.

Abstract

We have identified one frameshift mutation, one splice-site mutation, and two missense mutations in highly conserved residues in ZDHHC9 at Xq26.1 in 4 of 250 families with X-linked mental retardation (XLMR). In three of the families, the mental retardation phenotype is associated with a Marfanoid habitus, although none of the affected individuals meets the Ghent criteria for Marfan syndrome. ZDHHC9 is a palmitoyltransferase that catalyzes the posttranslational modification of NRAS and HRAS. The degree of palmitoylation determines the temporal and spatial location of these proteins in the plasma membrane and Golgi complex. The finding of mutations in ZDHHC9 suggests that alterations in the concentrations and cellular distribution of target proteins are sufficient to cause disease. This is the first XLMR gene to be reported that encodes a posttranslational modification enzyme, palmitoyltransferase. Furthermore, now that the first palmitoyltransferase that causes mental retardation has been identified, defects in other palmitoylation transferases become good candidates for causing other mental retardation syndromes.

Publication types

  • Case Reports
  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Acyltransferases / genetics*
  • Acyltransferases / metabolism
  • Amino Acid Sequence
  • Base Sequence
  • DNA / genetics
  • Female
  • Humans
  • Male
  • Marfan Syndrome / complications*
  • Marfan Syndrome / enzymology
  • Marfan Syndrome / genetics*
  • Mental Retardation, X-Linked / complications*
  • Mental Retardation, X-Linked / enzymology
  • Mental Retardation, X-Linked / genetics*
  • Molecular Sequence Data
  • Mutation*
  • Pedigree
  • Phenotype
  • Sequence Homology, Amino Acid
  • ras Proteins / metabolism

Substances

  • DNA
  • Acyltransferases
  • ZDHHC9 protein, human
  • ras Proteins

Associated data

  • OMIM/115150
  • OMIM/163950
  • OMIM/218040
  • RefSeq/NP_057116