Molecular imaging of the efficacy of heat shock protein 90 inhibitors in living subjects

Cancer Res. 2008 Jan 1;68(1):216-26. doi: 10.1158/0008-5472.CAN-07-2268.

Abstract

Heat shock protein 90 alpha (Hsp90 alpha)/p23 and Hsp90 beta/p23 interactions are crucial for proper folding of proteins involved in cancer and neurodegenerative diseases. Small molecule Hsp90 inhibitors block Hsp90 alpha/p23 and Hsp90 beta/p23 interactions in part by preventing ATP binding to Hsp90. The importance of isoform-selective Hsp90 alpha/p23 and Hsp90 beta/p23 interactions in determining the sensitivity to Hsp90 was examined using 293T human kidney cancer cells stably expressing split Renilla luciferase (RL) reporters. Interactions between Hsp90 alpha/p23 and Hsp90 beta/p23 in the split RL reporters led to complementation of RL activity, which was determined by bioluminescence imaging of intact cells in cell culture and living mice using a cooled charge-coupled device camera. The three geldanamycin-based and seven purine-scaffold Hsp90 inhibitors led to different levels of inhibition of complemented RL activities (10-70%). However, there was no isoform selectivity to both classes of Hsp90 inhibitors in cell culture conditions. The most potent Hsp90 inhibitor, PU-H71, however, led to a 60% and 30% decrease in RL activity (14 hr) in 293T xenografts expressing Hsp90 alpha/p23 and Hsp90 beta/p23 split reporters respectively, relative to carrier control-treated mice. Molecular imaging of isoform-specific Hsp90 alpha/p23 and Hsp90 beta/p23 interactions and efficacy of different classes of Hsp90 inhibitors in living subjects have been achieved with a novel genetically encoded reporter gene strategy that should help in accelerating development of potent and isoform-selective Hsp90 inhibitors.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Animals
  • Antineoplastic Agents / chemistry
  • Antineoplastic Agents / pharmacology*
  • Benzodioxoles / pharmacology*
  • Benzoquinones / chemistry
  • Cell Line, Tumor
  • Drug Screening Assays, Antitumor / methods*
  • Genes, Reporter / genetics
  • HSP90 Heat-Shock Proteins / antagonists & inhibitors*
  • HSP90 Heat-Shock Proteins / genetics
  • HSP90 Heat-Shock Proteins / metabolism
  • Humans
  • Lactams, Macrocyclic / chemistry
  • Luciferases, Renilla / analysis
  • Luciferases, Renilla / genetics
  • Mice
  • Molecular Chaperones / antagonists & inhibitors*
  • Molecular Chaperones / metabolism
  • Mutation
  • Phosphoproteins / antagonists & inhibitors*
  • Phosphoproteins / metabolism
  • Prostaglandin-E Synthases
  • Protein Interaction Mapping / methods
  • Purines / metabolism
  • Purines / pharmacology*
  • Xenograft Model Antitumor Assays

Substances

  • Antineoplastic Agents
  • Benzodioxoles
  • Benzoquinones
  • HSP90 Heat-Shock Proteins
  • HSP90AB1 protein, human
  • Lactams, Macrocyclic
  • Molecular Chaperones
  • Phosphoproteins
  • Purines
  • 9H-purine-9-propanamine, 6-amino-8-((6-iodo-1,3-benzodioxol-5-yl)thio)-N-(1-methylethyl)-
  • Luciferases, Renilla
  • PTGES3 protein, human
  • Prostaglandin-E Synthases
  • geldanamycin