Dual inhibition of PI3Kalpha and mTOR as an alternative treatment for Kaposi's sarcoma

Cancer Res. 2008 Oct 15;68(20):8361-8. doi: 10.1158/0008-5472.CAN-08-0878.

Abstract

Rapamycin (or sirolimus), the prototypical inhibitor of the mammalian target of rapamycin (mTOR) and an immunosuppressant used for the prevention of renal transplant rejection, has recently emerged as an effective treatment for Kaposi's sarcoma (KS), an enigmatic vascular tumor and a model for pathologic angiogenesis. Indeed, recent work supports a role for mTOR as a central player in the transformation of endothelial cells by the KS-associated herpesvirus-encoded G protein-coupled receptor (vGPCR), the viral oncogene believed to be responsible for causing KS. However, emerging evidence that rapamycin may transiently promote the activation of Akt may limit its use as an anti-KS therapy. Here, we show that activation of Akt in endothelial cells expressing vGPCR is augmented by treatment with rapamycin, resulting in the up-regulation of several Akt proliferative and survival pathways. However, use of a novel dual phosphatidylinositol 3-kinase alpha (PI3Kalpha)/mTOR inhibitor, PI-103, effectively and independently blocked activation of both PI3K and mTOR in vGPCR-expressing endothelial cells. This resulted in more effective inhibition of endothelial cell proliferation and survival in vitro and tumor growth in vivo. Our results suggest that PI-103 may be an effective therapeutic option for the treatment of patients with KS. Moreover, as KS may serve as a model for pathologic angiogenesis, our results further provide the basis for the early assessment of PI-103 as an antiangiogenic chemotherapeutic.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Angiogenesis Inhibitors / pharmacology
  • Animals
  • Antineoplastic Agents / pharmacology*
  • Apoptosis / drug effects
  • Cell Line
  • Cell Proliferation / drug effects
  • Endothelial Cells / drug effects
  • Furans / pharmacology*
  • Furans / therapeutic use
  • Immunosuppressive Agents / pharmacology
  • Mice
  • Neoplasm Transplantation
  • Phosphoinositide-3 Kinase Inhibitors*
  • Protein Kinases / drug effects*
  • Protein Kinases / physiology
  • Proto-Oncogene Proteins c-akt / physiology
  • Pyridines / pharmacology*
  • Pyridines / therapeutic use
  • Pyrimidines / pharmacology*
  • Pyrimidines / therapeutic use
  • Receptors, G-Protein-Coupled / analysis
  • Receptors, G-Protein-Coupled / physiology
  • Sarcoma, Kaposi / drug therapy*
  • Signal Transduction / drug effects
  • Sirolimus / pharmacology*
  • TOR Serine-Threonine Kinases
  • Transplantation, Homologous

Substances

  • Angiogenesis Inhibitors
  • Antineoplastic Agents
  • Furans
  • Immunosuppressive Agents
  • PI103
  • Phosphoinositide-3 Kinase Inhibitors
  • Pyridines
  • Pyrimidines
  • Receptors, G-Protein-Coupled
  • Protein Kinases
  • mTOR protein, mouse
  • Proto-Oncogene Proteins c-akt
  • TOR Serine-Threonine Kinases
  • Sirolimus