Dexamethasone palmitate successfully attenuates hemophagocytic syndrome after allogeneic stem cell transplantation: macrophage-targeted steroid therapy

Int J Hematol. 2012 Apr;95(4):428-33. doi: 10.1007/s12185-012-1023-z. Epub 2012 Feb 15.

Abstract

Hemophagocytic syndrome (HPS) induced by uncontrolled macrophage activation and subsequent graft failure is a frequent and prominent complication after allogeneic stem cell transplantation (allo-SCT), a cause of severe morbidity and death, and a therapeutic challenge. Liposome-incorporated dexamethasone, dexamethasone palmitate (DP), shows greater efficacy against macrophages as compared to dexamethasone sodium phosphate (DSP). Based on our findings that DP achieves significantly larger decrease than DSP on the viability of primary human macrophages compared in vitro, we tested the effects of DP in patients with HPS. A decrease in number of macrophages in the bone marrow and prevention of engraftment failure were observed in all patients without any severe complications. In conclusion, these data provide a rationale for testing DP as a first-line treatment for patients with HPS after allo-SCT.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adult
  • Cell Survival / drug effects
  • Cells, Cultured
  • Dexamethasone / analogs & derivatives*
  • Dexamethasone / therapeutic use
  • Female
  • Glucocorticoids / therapeutic use*
  • Humans
  • Lymphohistiocytosis, Hemophagocytic / drug therapy*
  • Lymphohistiocytosis, Hemophagocytic / etiology*
  • Lymphohistiocytosis, Hemophagocytic / pathology
  • Macrophages / drug effects*
  • Macrophages / pathology
  • Male
  • Middle Aged
  • Stem Cell Transplantation / adverse effects*
  • Transplantation, Homologous

Substances

  • Glucocorticoids
  • dexamethasone 21-palmitate
  • Dexamethasone