Ten challenges in the management of neuroblastoma

Future Oncol. 2012 Jul;8(7):839-58. doi: 10.2217/fon.12.70.

Abstract

Neuroblastoma is a complex disease with many contradictions and challenges. It is, by and large, a cancer of babies and preschool children, but it does occur, albeit increasingly rarely, in older children, adolescents and young adults. The prognosis is very variable, with outcome related to age, stage and molecular pathology. Neuroblastoma may behave in an almost benign way, with spontaneous regression in some infants, but the majority of older patients have high-risk disease, which is usually fatal, despite best current treatments. As a rare disease, international collaboration is essential to run clinical trials of adequate statistical power to answer important questions in a reasonable time frame. High-risk disease requires multimodality therapy including chemotherapy, surgery and radiotherapy as well as biological and immunological treatments for optimal outcomes. Innovative treatment approaches, sometimes associated with appreciable toxicity, offer hope for the future but, despite parental wishes, cannot be generally implemented without adequate assessment in clinical trials.

Publication types

  • Research Support, Non-U.S. Gov't
  • Review

MeSH terms

  • Adolescent
  • Age Factors
  • Antineoplastic Agents / adverse effects
  • Antineoplastic Agents / therapeutic use
  • Central Nervous System Neoplasms / pathology
  • Central Nervous System Neoplasms / therapy
  • Child
  • Child, Preschool
  • Combined Modality Therapy
  • Humans
  • Immunotherapy / methods
  • Neoplasm Staging
  • Neuroblastoma / epidemiology
  • Neuroblastoma / mortality
  • Neuroblastoma / pathology*
  • Neuroblastoma / therapy*
  • Neutropenia / etiology
  • Prognosis
  • Radiotherapy / methods
  • Rare Diseases
  • Survival Rate
  • Treatment Outcome

Substances

  • Antineoplastic Agents