Chemogenetic profiling identifies RAD17 as synthetically lethal with checkpoint kinase inhibition

Oncotarget. 2015 Nov 3;6(34):35755-69. doi: 10.18632/oncotarget.5928.

Abstract

Chemical inhibitors of the checkpoint kinases have shown promise in the treatment of cancer, yet their clinical utility may be limited by a lack of molecular biomarkers to identify specific patients most likely to respond to therapy. To this end, we screened 112 known tumor suppressor genes for synthetic lethal interactions with inhibitors of the CHEK1 and CHEK2 checkpoint kinases. We identified eight interactions, including the Replication Factor C (RFC)-related protein RAD17. Clonogenic assays in RAD17 knockdown cell lines identified a substantial shift in sensitivity to checkpoint kinase inhibition (3.5-fold) as compared to RAD17 wild-type. Additional evidence for this interaction was found in a large-scale functional shRNA screen of over 100 genotyped cancer cell lines, in which CHEK1/2 mutant cell lines were unexpectedly sensitive to RAD17 knockdown. This interaction was widely conserved, as we found that RAD17 interacts strongly with checkpoint kinases in the budding yeast Saccharomyces cerevisiae. In the setting of RAD17 knockdown, CHEK1/2 inhibition was found to be synergistic with inhibition of WEE1, another pharmacologically relevant checkpoint kinase. Accumulation of the DNA damage marker γH2AX following chemical inhibition or transient knockdown of CHEK1, CHEK2 or WEE1 was magnified by knockdown of RAD17. Taken together, our data suggest that CHEK1 or WEE1 inhibitors are likely to have greater clinical efficacy in tumors with RAD17 loss-of-function.

Keywords: DNA damage; RAD17; biomarker; checkpoint kinase inhibitor; synthetic lethal.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Antineoplastic Agents / pharmacology*
  • Biomarkers, Pharmacological / metabolism
  • Cell Cycle / drug effects
  • Cell Cycle / genetics
  • Cell Cycle Proteins / genetics
  • Cell Cycle Proteins / metabolism*
  • Checkpoint Kinase 1
  • Checkpoint Kinase 2 / genetics
  • Checkpoint Kinase 2 / metabolism
  • DNA Damage / drug effects
  • DNA Damage / genetics
  • DNA-Binding Proteins / genetics
  • DNA-Binding Proteins / metabolism*
  • Drug Discovery
  • HeLa Cells
  • Humans
  • Molecular Targeted Therapy
  • Mutation / genetics
  • Neoplasms / diagnosis
  • Neoplasms / drug therapy*
  • Nuclear Proteins / genetics
  • Nuclear Proteins / metabolism*
  • Protein Kinases / genetics
  • Protein Kinases / metabolism
  • Protein-Tyrosine Kinases / genetics
  • Protein-Tyrosine Kinases / metabolism
  • RNA, Small Interfering / genetics
  • Saccharomyces cerevisiae / pathogenicity*
  • Saccharomyces cerevisiae / physiology*
  • Saccharomyces cerevisiae Proteins / genetics
  • Saccharomyces cerevisiae Proteins / metabolism*
  • Thiophenes / pharmacology*
  • Urea / analogs & derivatives*
  • Urea / pharmacology

Substances

  • 3-(carbamoylamino)-5-(3-fluorophenyl)-N-(3-piperidyl)thiophene-2-carboxamide
  • Antineoplastic Agents
  • Biomarkers, Pharmacological
  • Cell Cycle Proteins
  • DNA-Binding Proteins
  • Nuclear Proteins
  • RAD17 protein, S cerevisiae
  • RNA, Small Interfering
  • Rad17 protein, human
  • Saccharomyces cerevisiae Proteins
  • Thiophenes
  • Urea
  • Protein Kinases
  • SWE1 protein, S cerevisiae
  • Checkpoint Kinase 2
  • Protein-Tyrosine Kinases
  • CHEK1 protein, human
  • Checkpoint Kinase 1