Mammalian cell transient expression, non-affinity purification, and characterization of human recombinant IGFBP7, an IGF-1 targeting therapeutic protein

Int Immunopharmacol. 2015 Dec;29(2):476-487. doi: 10.1016/j.intimp.2015.10.008. Epub 2015 Oct 23.

Abstract

Targeted inhibiting insulin-like growth factor 1 is an effective approach for cancer therapy. Insulin-like growth factor binding protein 7 (IGFBP7) is considered as a potential therapeutic protein. However, producing high quality of such non-IgG proteins in mammalian cells is still a challenge in biopharmaceutical development. Here, we report a rapid production process by using transient gene transfection in HEK 293E cells. A set of constructs combining several expression promoters, leader sequences, and 5' un-translated regions were generated and optimized, from which the best vector with expression level at ~50mg/L was selected for production at 2L cell culture scale. Comparison study in downstream purification methods led to development of a scalable, non-affinity chromatography strategy through Super Q, Fast Flow Q, and Heparin columns. The product was characterized in purity (99%), isoelectric point, molecule weight, glycosylation, and stability by using SEC-HPLC, SDS-PAGE, isoelectric focusing and mass spectrometry. The highly purified product shows IGF-1 binding activity and inhibits IGF-1-induced cell proliferation. This process not only provides a remarkable high expression at ~50mg/L and pure glycosylated mammalian rhIGFBP7, also highlights that transient gene expression technology is practical to be used for production and early development of recombinant non-IgG therapeutic proteins.

Keywords: IGFBP7; Protein expression; Protein purification; Transient gene expression.

Publication types

  • Research Support, N.I.H., Extramural

MeSH terms

  • 5' Untranslated Regions / genetics
  • Amino Acid Sequence
  • Cell Proliferation / drug effects
  • Gene Expression / drug effects
  • Genetic Vectors
  • Glycosylation
  • HEK293 Cells
  • Humans
  • Insulin-Like Growth Factor Binding Proteins / biosynthesis
  • Insulin-Like Growth Factor Binding Proteins / genetics*
  • Insulin-Like Growth Factor Binding Proteins / pharmacology*
  • Insulin-Like Growth Factor I / drug effects*
  • Molecular Sequence Data
  • Recombinant Proteins / pharmacology
  • Transfection

Substances

  • 5' Untranslated Regions
  • Insulin-Like Growth Factor Binding Proteins
  • Recombinant Proteins
  • insulin-like growth factor binding protein-related protein 1
  • Insulin-Like Growth Factor I