Economic and care considerations of Marfan syndrome

Expert Rev Pharmacoecon Outcomes Res. 2016 Oct;16(5):591-598. doi: 10.1080/14737167.2016.1240619. Epub 2016 Oct 6.

Abstract

Marfan syndrome is a rare multisystem disease of the connective tissue, which affects multiple organ systems. advances in healthcare have doubled the life-expectancy of patients over the past three decades. to date, there is no comprehensive review that consolidates economic considerations and care for marfan patients. Areas covered: Present research suggests that there may be a link between treatment pattern, disease progression and economic costs of Marfan syndrome. It indicates that an early detection of the disease and preventive interventions achieve a dual aim. From a patient perspective, it may reduce the amount of emergency surgery or intervention, and inpatient stays. In addition, it slows disease progression, lowers lifestyle restrictions, reduces psychological stress, and improves health-related quality of life. Expert commentary: Early detection and preventive measures are likely to achieve a dual aim by simultaneously containing costs and reducing the number and length of inpatient stays.

Keywords: FBN1; Loeys-Dietz syndrome; Marfan syndrome; TGFBR2; costs; decision-making; economy; gene; healthcare; surgery.

Publication types

  • Review

MeSH terms

  • Disease Progression
  • Health Care Costs*
  • Hospitalization / statistics & numerical data
  • Humans
  • Length of Stay
  • Life Expectancy
  • Life Style
  • Marfan Syndrome / economics
  • Marfan Syndrome / physiopathology
  • Marfan Syndrome / therapy*
  • Quality of Life*
  • Stress, Psychological / etiology