High-Affinity α-Conotoxin PnIA Analogs Designed on the Basis of the Protein Surface Topography Method

Sci Rep. 2016 Nov 14:6:36848. doi: 10.1038/srep36848.

Abstract

Despite some success for small molecules, elucidating structure-function relationships for biologically active peptides - the ligands for various targets in the organism - remains a great challenge and calls for the development of novel approaches. Some of us recently proposed the Protein Surface Topography (PST) approach, which benefits from a simplified representation of biomolecules' surface as projection maps, which enables the exposure of the structure-function dependencies. Here, we use PST to uncover the "activity pattern" in α-conotoxins - neuroactive peptides that effectively target nicotinic acetylcholine receptors (nAChRs). PST was applied in order to design several variants of the α-conotoxin PnIA, which were synthesized and thoroughly studied. Among the best was PnIA[R9, L10], which exhibits nanomolar affinity for the α7 nAChR, selectivity and a slow wash-out from this target. Importantly, these mutations could hardly be delineated by "standard" structure-based drug design. The proposed combination of PST with a set of experiments proved very efficient for the rational construction of new bioactive molecules.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Allosteric Site
  • Animals
  • Circular Dichroism
  • Computer Simulation
  • Conotoxins / chemical synthesis*
  • Conotoxins / chemistry
  • Conotoxins / genetics
  • Conotoxins / pharmacology*
  • Drug Design
  • Humans
  • Molecular Dynamics Simulation
  • Mutation
  • Structure-Activity Relationship
  • alpha7 Nicotinic Acetylcholine Receptor / metabolism*

Substances

  • Conotoxins
  • alpha-conotoxin PnIA
  • alpha7 Nicotinic Acetylcholine Receptor