Structure-Based Drug Design of Mineralocorticoid Receptor Antagonists to Explore Oxosteroid Receptor Selectivity

ChemMedChem. 2017 Jan 5;12(1):50-65. doi: 10.1002/cmdc.201600529. Epub 2016 Dec 15.

Abstract

The mineralocorticoid receptor (MR) is a nuclear hormone receptor involved in the regulation of body fluid and electrolyte homeostasis. In this study we explore selectivity triggers for a series of nonsteroidal MR antagonists to improve selectivity over other members of the oxosteroid receptor family. A biaryl sulfonamide compound was identified in a high-throughput screening (HTS) campaign. The compound bound to MR with pKi =6.6, but displayed poor selectivity over the glucocorticoid receptor (GR) and the progesterone receptor (PR). Following X-ray crystallography of MR in complex with the HTS hit, a compound library was designed that explored an induced-fit hypothesis that required movement of the Met852 side chain. An improvement in MR selectivity of 11- to 79-fold over PR and 23- to 234-fold over GR was obtained. Given the U-shaped binding conformation, macrocyclizations were explored, yielding a macrocycle that bound to MR with pKi =7.3. Two protein-ligand X-ray structures were determined, confirming the hypothesized binding mode for the designed compounds.

Keywords: NR3C2; drug design; macrocycles; nuclear hormone receptors; structure-based drug design.

MeSH terms

  • Dose-Response Relationship, Drug
  • Drug Design*
  • High-Throughput Screening Assays
  • Humans
  • Mineralocorticoid Receptor Antagonists / chemical synthesis
  • Mineralocorticoid Receptor Antagonists / chemistry*
  • Mineralocorticoid Receptor Antagonists / pharmacology*
  • Models, Molecular
  • Molecular Structure
  • Receptors, Glucocorticoid / chemistry*
  • Receptors, Glucocorticoid / metabolism*
  • Receptors, Mineralocorticoid / metabolism*
  • Structure-Activity Relationship
  • Substrate Specificity

Substances

  • Mineralocorticoid Receptor Antagonists
  • Receptors, Glucocorticoid
  • Receptors, Mineralocorticoid