Systematic In Vivo Inactivation of Chromatin-Regulating Enzymes Identifies Setd2 as a Potent Tumor Suppressor in Lung Adenocarcinoma

Cancer Res. 2017 Apr 1;77(7):1719-1729. doi: 10.1158/0008-5472.CAN-16-2159. Epub 2017 Feb 15.

Abstract

Chromatin-modifying genes are frequently mutated in human lung adenocarcinoma, but the functional impact of these mutations on disease initiation and progression is not well understood. Using a CRISPR-based approach, we systematically inactivated three of the most commonly mutated chromatin regulatory genes in two KrasG12D-driven mouse models of lung adenocarcinoma to characterize the impact of their loss. Targeted inactivation of SWI/SNF nucleosome-remodeling complex members Smarca4 (Brg1) or Arid1a had complex effects on lung adenocarcinoma initiation and progression. Loss of either Brg1 or Arid1a were selected against in early-stage tumors, but Brg1 loss continued to limit disease progression over time, whereas loss of Arid1a eventually promoted development of higher grade lesions. In contrast to these stage-specific effects, loss of the histone methyltransferase Setd2 had robust tumor-promoting consequences. Despite disparate impacts of Setd2 and Arid1a loss on tumor development, each resulted in a gene expression profile with significant overlap. Setd2 inactivation and subsequent loss of H3K36me3 led to the swift expansion and accelerated progression of both early- and late-stage tumors. However, Setd2 loss per se was insufficient to overcome a p53-regulated barrier to malignant progression, nor establish the prometastatic cellular states that stochastically evolve during lung adenocarcinoma progression. Our study uncovers differential and context-dependent effects of SWI/SNF complex member loss, identifies Setd2 as a potent tumor suppressor in lung adenocarcinoma, and establishes model systems to facilitate further study of chromatin deregulation in lung cancer. Cancer Res; 77(7); 1719-29. ©2017 AACR.

MeSH terms

  • Adenocarcinoma / etiology
  • Adenocarcinoma / prevention & control*
  • Adenocarcinoma of Lung
  • Animals
  • Chromatin / physiology*
  • Clustered Regularly Interspaced Short Palindromic Repeats
  • DNA Helicases / physiology
  • DNA-Binding Proteins
  • HEK293 Cells
  • Histone-Lysine N-Methyltransferase / physiology*
  • Humans
  • Lung Neoplasms / etiology
  • Lung Neoplasms / prevention & control*
  • Mice
  • Mice, Inbred C57BL
  • Mutation
  • Nuclear Proteins / physiology
  • Proto-Oncogene Proteins p21(ras) / genetics
  • Transcription Factors / physiology
  • Tumor Suppressor Protein p53 / physiology
  • Tumor Suppressor Proteins / physiology*

Substances

  • ARID1A protein, human
  • Chromatin
  • DNA-Binding Proteins
  • KRAS protein, human
  • Nuclear Proteins
  • Transcription Factors
  • Tumor Suppressor Protein p53
  • Tumor Suppressor Proteins
  • Histone-Lysine N-Methyltransferase
  • SETD2 protein, human
  • SMARCA4 protein, human
  • DNA Helicases
  • Proto-Oncogene Proteins p21(ras)