Clinical-grade generation of peptide-stimulated CMV/EBV-specific T cells from G-CSF mobilized stem cell grafts

J Transl Med. 2018 May 9;16(1):124. doi: 10.1186/s12967-018-1498-3.

Abstract

Background: A major complication after allogeneic hematopoietic stem cell transplantation (aSCT) is the reactivation of herpesviruses such as cytomegalovirus (CMV) and Epstein-Barr virus (EBV). Both viruses cause significant mortality and compromise quality of life after aSCT. Preventive transfer of virus-specific T cells can suppress reactivation by re-establishing functional antiviral immune responses in immunocompromised hosts.

Methods: We have developed a good manufacturing practice protocol to generate CMV/EBV-peptide-stimulated T cells from leukapheresis products of G-CSF mobilized and non-mobilized donors. Our procedure selectively expands virus-specific CD8+ und CD4+ T cells over 9 days using a generic pool of 34 CMV and EBV peptides that represent well-defined dominant T-cell epitopes with various HLA restrictions. For HLA class I, this set of peptides covers at least 80% of the European population.

Results: CMV/EBV-specific T cells were successfully expanded from leukapheresis material of both G-CSF mobilized and non-mobilized donors. The protocol allows administration shortly after stem cell transplantation (d30+), storage over liquid nitrogen for iterated applications, and protection of the stem cell donor by avoiding a second leukapheresis.

Conclusion: Our protocol allows for rapid and cost-efficient production of T cells for early transfusion after aSCT as a preventive approach. It is currently evaluated in a phase I/IIa clinical trial.

Keywords: Adoptive transfer; Allogeneic; CMV; EBV; Reactivation; Stem cell transplantation; T cell.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Alleles
  • Amino Acid Sequence
  • Cell Proliferation / drug effects
  • Cytokines / metabolism
  • Cytomegalovirus / physiology*
  • Granulocyte Colony-Stimulating Factor / pharmacology*
  • HLA Antigens / genetics
  • Hematopoietic Stem Cell Mobilization*
  • Hematopoietic Stem Cell Transplantation*
  • Herpesvirus 4, Human / physiology*
  • Humans
  • Lymphocyte Activation / drug effects
  • Peptides / chemistry
  • Peptides / pharmacology*
  • T-Lymphocytes / drug effects
  • T-Lymphocytes / immunology*
  • Tissue Donors

Substances

  • Cytokines
  • HLA Antigens
  • Peptides
  • Granulocyte Colony-Stimulating Factor