Fixing the Unfixable: The Art of Optimizing Natural Products for Human Medicine

J Med Chem. 2019 Sep 26;62(18):8412-8428. doi: 10.1021/acs.jmedchem.9b00246. Epub 2019 Apr 26.

Abstract

Molecules isolated from natural sources including bacteria, fungi, and plants are a long-standing source of therapeutics that continue to add to our medicinal arsenal today. Despite their potency and prominence in the clinic, complex natural products often exhibit a number of liabilities that hinder their development as therapeutics, which may be partially responsible for the current trend away from natural product discovery, research, and development. However, advances in synthetic biology and organic synthesis have inspired a new generation of natural product chemists to tackle powerful undeveloped scaffolds. In this Perspective, we will present case studies demonstrating the historical and current focus on making targeted, but significant, changes to natural product scaffolds via biosynthetic gene cluster manipulation, total synthesis, semisynthesis, or a combination of these methods, with a focus on increasing activity, decreasing toxicity, or improving chemical and pharmacological properties.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, U.S. Gov't, Non-P.H.S.
  • Review

MeSH terms

  • Anti-Bacterial Agents / pharmacology
  • Benzoquinones / pharmacology
  • Biological Products / pharmacology*
  • Cell Line, Tumor
  • Chemistry, Organic
  • Chemistry, Pharmaceutical / trends
  • Glycopeptides / chemistry
  • Humans
  • Lactams, Macrocyclic / pharmacology
  • Macrolides / pharmacology
  • Multigene Family
  • Neoplasms / drug therapy*
  • Pactamycin / pharmacology
  • Peptides / pharmacology
  • Polyenes / chemistry
  • Synthetic Biology / trends
  • Tetracyclines / pharmacology

Substances

  • Anti-Bacterial Agents
  • Benzoquinones
  • Biological Products
  • Glycopeptides
  • Lactams, Macrocyclic
  • Macrolides
  • Peptides
  • Polyenes
  • Tetracyclines
  • Pactamycin
  • geldanamycin