Feasibility of thiotepa addition to the fludarabine-busulfan conditioning with tacrolimus/sirolimus as graft vs host disease prophylaxis

Leuk Lymphoma. 2020 Aug;61(8):1823-1832. doi: 10.1080/10428194.2020.1788015. Epub 2020 Jul 11.

Abstract

In classical reduced-intensity conditioning (RIC) regimens, including the fludarabine and busulphan (BF) combination, sirolimus and tacrolimus (SIR-TAC) as graft vs host disease (GVHD) prophylaxis has shown acceptable results. The outcomes of SIR-TAC in a more intense RIC regimen as Thiotepa-fludarabine-busulfan (TBF) have been hardly investigated. This retrospective study included all consecutive patients receiving an allogeneic hematopoietic stem cell transplantation for myeloid malignancies (January 2009-2017) conditioned with either TBF or BF and receiving SIR-TAC. Patients receiving TBF presented higher non-relapse mortality (31.6 vs 12.3%, p = .01), along with shorter overall survival (51.8% vs 77.8%, p < .01) at 2 years than patients treated with BF. There were no significant differences in the cumulative incidence of grade II-IV acute GVHD or moderate-severe chronic GVHD or relapse between both groups. These results suggest that TBF does not seem to improve the traditional RIC BF regimen, at least when associated with SIR-TAC prophylaxis.

Keywords: Thiotepa-fludarabine-busulfan; allogeneic hematopoietic cell transplantation; graft vs host disease prophylaxis; reduce intensity conditioning; sirolimus and tacrolimus.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Busulfan
  • Feasibility Studies
  • Graft vs Host Disease* / etiology
  • Graft vs Host Disease* / prevention & control
  • Hematopoietic Stem Cell Transplantation* / adverse effects
  • Humans
  • Retrospective Studies
  • Sirolimus
  • Tacrolimus
  • Thiotepa
  • Transplantation Conditioning
  • Vidarabine / analogs & derivatives

Substances

  • Thiotepa
  • Vidarabine
  • Busulfan
  • fludarabine
  • Sirolimus
  • Tacrolimus