PARP inhibition is a modulator of anti-tumor immune response in BRCA-deficient tumors

Oncoimmunology. 2022 Jun 18;11(1):2083755. doi: 10.1080/2162402X.2022.2083755. eCollection 2022.

Abstract

PARP inhibitors are synthetically lethal with BRCA1/2 mutations, and in this setting, accumulation of DNA damage leads to cell death. Because increased DNA damage and subsequent immune activation can prime an anti-tumor immune response, we studied the impact of olaparib ± immune checkpoint blockade (ICB) on anti-tumor activity and the immune microenvironment. Concurrent combination of olaparib, at clinically relevant exposures, with ICB gave durable and deeper anti-tumor activity in the Brca1m BR5 model vs. monotherapies. Olaparib and combination treatment modulated the immune microenvironment, including increases in CD8+ T cells and NK cells, and upregulation of immune pathways, including type I IFN and STING signaling. Olaparib also induced a dose-dependent upregulation of immune pathways, including JAK/STAT, STING and type I IFN, in the tumor cell compartment of a BRCA1m (HBCx-10) but not a BRCA WT (HBCx-9) breast PDX model. In vitro, olaparib induced BRCAm tumor cell-specific dendritic cell transactivation. Relevance to human disease was assessed using patient samples from the MEDIOLA (NCT02734004) trial, which showed increased type I IFN, STING, and JAK/STAT pathway expression following olaparib treatment, in line with preclinical findings. These data together provide evidence for a mechanism and schedule underpinning potential benefit of ICB combination with olaparib.

Keywords: BRCA; PARP inhibitor; cGAS-STING; immune checkpoint blockade; olaparib.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • BRCA1 Protein / genetics
  • BRCA1 Protein / metabolism
  • Clinical Trials as Topic
  • Female
  • Humans
  • Immunity
  • Janus Kinases / metabolism
  • Janus Kinases / pharmacology
  • Janus Kinases / therapeutic use
  • Ovarian Neoplasms* / drug therapy
  • Poly(ADP-ribose) Polymerase Inhibitors* / pharmacology
  • Poly(ADP-ribose) Polymerase Inhibitors* / therapeutic use
  • STAT Transcription Factors / metabolism
  • STAT Transcription Factors / pharmacology
  • STAT Transcription Factors / therapeutic use
  • Signal Transduction
  • Tumor Microenvironment

Substances

  • BRCA1 Protein
  • Poly(ADP-ribose) Polymerase Inhibitors
  • STAT Transcription Factors
  • Janus Kinases

Associated data

  • ClinicalTrials.gov/NCT02734004

Grants and funding

This study was funded by AstraZeneca.