A first-in-human, randomized study of the safety, pharmacokinetics and pharmacodynamics of povetacicept, an enhanced dual BAFF/APRIL antagonist, in healthy adults

Clin Transl Sci. 2024 Nov;17(11):e70055. doi: 10.1111/cts.70055.

Abstract

Therapeutic agents targeting the tumor necrosis factor (TNF) superfamily cytokines B-cell activating factor (BAFF, BLyS) and/or A PRoliferation Inducing Ligand (APRIL) have demonstrated clinical effectiveness in multiple autoimmune diseases, such as systemic lupus erythematosus, lupus nephritis, and immunoglobulin A nephropathy (IgAN). However, their clinical utility can often be limited by incomplete and/or prolonged times to clinical response and inconvenient dosing regimens, which may be improved by more potent dual inhibition of both cytokines. Povetacicept (ALPN-303; TACI vTD-Fc) is a crystallizable fragment (Fc) fusion protein of an engineered transmembrane activator and CAML interactor (TACI) domain which mediates more potent inhibitory activity than wild-type TACI-Fc or BAFF- or APRIL-specific antibodies and demonstrates superior pharmacokinetic and pharmacodynamic activity in multiple preclinical disease models. In this first-in-human study in healthy adults, povetacicept was well-tolerated as single ascending doses of up to 960 mg administered intravenously or subcutaneously. Dose-dependent pharmacokinetics were observed. Coverage of BAFF and APRIL was observed for 2-3 weeks and ≥4 weeks after doses of 80 mg and ≥240 mg, respectively. Maximal pharmacodynamic effects were observed at dose levels ≥80 mg for a single dose, associated with on-target reductions in antibody-secreting cells as well as in all circulating immunoglobulin isotypes, including the IgAN disease-related biomarker galactose-deficient-immunoglobulin A1 (Gd-IgA1), and were superior to results reported for wild-type TACI-Fc. These data strongly support further development of povetacicept for the treatment of B-cell-mediated automimmune diseases.

Publication types

  • Randomized Controlled Trial
  • Clinical Trial, Phase I

MeSH terms

  • Adult
  • B-Cell Activating Factor* / antagonists & inhibitors
  • B-Cell Activating Factor* / immunology
  • Dose-Response Relationship, Drug
  • Double-Blind Method
  • Female
  • Healthy Volunteers*
  • Humans
  • Male
  • Middle Aged
  • Recombinant Fusion Proteins* / administration & dosage
  • Recombinant Fusion Proteins* / adverse effects
  • Recombinant Fusion Proteins* / pharmacokinetics
  • Recombinant Fusion Proteins* / pharmacology
  • Transmembrane Activator and CAML Interactor Protein / immunology
  • Tumor Necrosis Factor Ligand Superfamily Member 13* / antagonists & inhibitors
  • Tumor Necrosis Factor Ligand Superfamily Member 13* / immunology
  • Young Adult

Substances

  • B-Cell Activating Factor
  • Tumor Necrosis Factor Ligand Superfamily Member 13
  • TNFSF13B protein, human
  • TNFSF13 protein, human
  • Recombinant Fusion Proteins
  • TACI receptor-IgG Fc fragment fusion protein
  • Transmembrane Activator and CAML Interactor Protein