Osteogenesis imperfecta and type-I collagen mutations. A lethal variant caused by a Gly910-->Ala substitution in the alpha 1 (I) chain

Eur J Biochem. 1993 Feb 1;211(3):415-9. doi: 10.1111/j.1432-1033.1993.tb17565.x.

Abstract

In this study we describe a new dominant point mutation in COL1A1 causing a lethal form of Osteogenesis imperfecta (type II B). Dermal cultured fibroblasts from the proband were shown to produce both normal and heavily overmodified type-I collagen. The mutation introduced a local conformational perturbation, which causes abnormal exposure of arginine residues; the triple helical domain was susceptible to trypsin digestion even at 30 degrees C. The chains bearing the point mutation were poorly secreted and short-term pulse experiments showed that the extensive intracellular retention of mutant trimers also impaired the secretion of normal chains. The molecular defect was localized in a COL1A1 allele by cloning and sequencing a cDNA region corresponding to the CB6 peptide. A G to C transversion which causes the substitution in the triple helical region of Gly910 with alanine was found. The mutation also causes the disappearance of a MspI-recognition site at nucleotide 3263 of the pro alpha 1 (I) coding sequence. Restriction analysis, along with the biochemical screening of collagens, allowed us to perform prenatal diagnosis on cells from chorionic-villus sampling and to exclude the recurrence of the mutation in the sibling.

Publication types

  • Case Reports
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Alanine / genetics*
  • Collagen / genetics*
  • Cyanogen Bromide
  • Deoxyribonuclease HpaII
  • Deoxyribonucleases, Type II Site-Specific
  • Electrophoresis, Polyacrylamide Gel
  • Female
  • Fibroblasts / metabolism
  • Glycine / genetics*
  • Humans
  • Infant, Newborn
  • Osteogenesis Imperfecta / genetics*
  • Peptide Mapping
  • Point Mutation*
  • Sequence Analysis, DNA
  • Trypsin / metabolism

Substances

  • Collagen
  • Deoxyribonuclease HpaII
  • Deoxyribonucleases, Type II Site-Specific
  • Trypsin
  • Alanine
  • Cyanogen Bromide
  • Glycine