Gene therapy for inherited neurological disorders: towards therapeutic intervention in the Lesch-Nyhan syndrome

Prog Brain Res. 1998:117:485-501. doi: 10.1016/s0079-6123(08)64034-0.
No abstract available

Publication types

  • Research Support, Non-U.S. Gov't
  • Review

MeSH terms

  • Animals
  • Brain / metabolism*
  • Brain / physiopathology
  • Gene Transfer Techniques
  • Genetic Therapy*
  • Humans
  • Hypoxanthine Phosphoribosyltransferase / genetics*
  • Hypoxanthine Phosphoribosyltransferase / metabolism
  • Lesch-Nyhan Syndrome / therapy*
  • Models, Chemical
  • Models, Neurological
  • Recombinant Proteins / metabolism

Substances

  • Recombinant Proteins
  • Hypoxanthine Phosphoribosyltransferase