Safety and efficacy of enzyme replacement therapy in combination with hematopoietic stem cell transplantation in Hurler syndrome.
Grewal SS, Wynn R, Abdenur JE, Burton BK, Gharib M, Haase C, Hayashi RJ, Shenoy S, Sillence D, Tiller GE, Dudek ME, van Royen-Kerkhof A, Wraith JE, Woodard P, Young GA, Wulffraat N, Whitley CB, Peters C.
Grewal SS, et al. Among authors: whitley cb.
Genet Med. 2005 Feb;7(2):143-6. doi: 10.1097/01.gim.0000154299.22120.6a.
Genet Med. 2005.
PMID: 15714083
Free article.
Clinical Trial.