Combination brain and systemic injections of AAV provide maximal functional and survival benefits in the Niemann-Pick mouse.
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Proc Natl Acad Sci U S A. 2007 May 29;104(22):9505-10. doi: 10.1073/pnas.0703509104. Epub 2007 May 21.
Proc Natl Acad Sci U S A. 2007.
PMID: 17517638
Free PMC article.