Type I SMA "new natural history": long-term data in nusinersen-treated patients.
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Ann Clin Transl Neurol. 2021 Mar;8(3):548-557. doi: 10.1002/acn3.51276. Epub 2021 Feb 6.
Ann Clin Transl Neurol. 2021.
PMID: 33547876
Free PMC article.