Retinal cells derived from patients with DRAM2-dependent CORD21 dystrophy exhibit key lysosomal enzyme deficiency and lysosomal content accumulation.
Tsikandelova R, Galo E, Cerniauskas E, Hallam D, Georgiou M, Cerna-Chavez R, Atkinson R, Palmowski P, Burté F, Davies T, Steel DH, McKibbin M, Bond J, Haggarty J, Whitfield P, Korolchuk V, Armstrong L, Yang C, Dorgau B, Kurzawa-Akanbi M, Lako M.
Tsikandelova R, et al. Among authors: mckibbin m.
Stem Cell Reports. 2024 Aug 13;19(8):1107-1121. doi: 10.1016/j.stemcr.2024.06.002. Epub 2024 Jul 3.
Stem Cell Reports. 2024.
PMID: 38964324
Free PMC article.